PTC Therapeutics, Inc. (PTCT) Financial Statements & Historical Data

PTC Therapeutics, Inc. (PTCT) — Price $67.23 HealthcareBiotechnology — NASDAQ

Latest reported results:

Detailed financial statements for PTC Therapeutics, Inc. (PTCT): income statement, balance sheet and cash-flow summary. Track margins, debt, liquidity and profitability trends year over year with up to 20 years of history.

PTC Therapeutics, Inc. (PTCT) is a biopharmaceutical company committed to the research, development, and commercialization of innovative therapies for patients afflicted with rare genetic disorders. Its robust pipeline encompasses both commercialized therapies and a variety of experimental drug candidates, spanning all stages of development—from early research and preclinical studies to clinical trials—with a primary focus on addressing various rare disease indications.

Analysis Summary

PTC Therapeutics, Inc. reported revenue of $1.73B in the most recent fiscal year, growing at a 5-year CAGR of 35.4%.

Trailing-twelve-month margins: gross margin 82.1%, operating margin 11.5%, net margin -3.8%.

At the current price of $67.23, PTCT has negative trailing earnings (P/E not meaningful) and an ROE of 21.72%. Market capitalisation stands at $5.6B.

Balance sheet quality for PTCT: current ratio of 2.3, net debt of $761.7M. A debt-to-equity below 1.0 typically signals conservative capital structure, while a current ratio above 1.5 indicates comfortable short-term liquidity.

Cash flow quality is below average: free cash flow of $411.2M represents 60% conversion of reported net income. High conversion (above 90%) suggests earnings translate cleanly into cash; lower conversion may indicate working capital tightness or accounting timing differences.

Income Statement (10y)

Year2016201720182019202020212022202320242025
Revenue$82.7M$194.4M$264.7M$307.0M$380.8M$538.6M$698.8M$937.8M$806.8M$1.73B
Cost of Revenue$117.6M$4.6M$12.7M$12.1M$18.9M$32.3M$44.7M$65.5M$57.4M$71.8M
Gross Profit-$34.9M$189.8M$252.1M$294.8M$361.8M$506.3M$654.1M$872.3M$749.4M$1.66B
Research & Development$117.6M$117.5M$172.0M$257.5M$477.6M$540.7M$651.5M$666.6M$534.5M$455.2M
Selling, General & Admin$97.1M$121.3M$153.5M$202.5M$245.2M$285.8M$326.0M$332.5M$300.9M$347.1M
Operating Expenses$214.8M$254.1M$348.4M$536.0M$793.6M$880.7M$1.10B$1.31B$1.05B$802.4M
Operating Income-$132.1M-$64.3M-$115.7M-$241.2M-$431.8M-$374.4M-$447.4M-$439.5M-$302.6M$856.5M
EBITDA-$128.8M-$46.6M-$89.5M-$195.3M-$303.1M-$368.2M-$367.8M-$330.3M-$120.5M$887.7M
Interest Expense$8.3M$12.1M$12.6M$12.5M$56.4M$86.0M$90.9M$129.2M$167.0M$152.2M
Pre-tax Income-$141.5M-$77.7M-$128.1M-$239.9M-$402.9M-$518.3M-$587.5M-$696.1M-$363.1M$696.6M
Income Tax$569000$1.3M-$29000$11.7M$35.2M$5.6M-$28.5M-$69.5M$176000$14.0M
Net Income-$142.1M-$79.0M-$128.1M-$251.6M-$438.2M-$523.9M-$559.0M-$626.6M-$363.3M$682.6M
EPS$-4.17$-2.02$-2.75$-4.27$-6.64$-7.43$-7.79$-8.37$-4.73$8.58
EPS (Diluted)$-4.17$-2.02$-2.75$-4.27$-6.64$-7.43$-7.79$-8.37$-4.73$7.78
Shares Outstanding (Diluted)$34.0M$39.2M$46.6M$58.9M$66.0M$70.5M$71.7M$74.8M$76.8M$88.3M

Income Statement (Quarterly)

Year2025-Q32025-Q42026-Q12026-Q2
Revenue$211.0M$164.7M$272.6M$360.5M
Gross Profit$95.1M$148.4M$244.5M$340.6M
Operating Income$3.0M-$81.6M$45.9M$149.0M
EBITDA$20.6M-$71.0M$62.0M$161.9M
Net Income$15.9M-$135.0M-$2.8M$83.5M
EPS$0.20$-1.67$-0.03$1.01
EPS (Diluted)$0.20$-1.67$-0.03$0.92

Balance Sheet (10y)

Year2016201720182019202020212022202320242025
Cash & Equivalents$231.7M$191.2M$227.6M$288.0M$208.8M$189.7M$279.8M$594.0M$779.7M$984.6M
Short-term Investments000$398.5M$894.8M$583.7M$130.9M$282.7M$360.0M$960.7M
Receivables$24.9M$40.4M$67.9M$55.5M$69.9M$110.5M$155.6M$160.8M$158.6M$181.6M
Inventory0$10.8M$16.1M$19.3M$18.7M$15.9M$21.8M$30.6M$23.2M$79.6M
Total Current Assets$261.3M$249.1M$320.9M$779.3M$1.23B$954.4M$693.8M$1.22B$1.37B$2.27B
Property, Plant & Equipment$7.4M$8.4M$12.7M$35.2M$118.2M$130.0M$175.0M$179.0M$117.7M$135.4M
Goodwill00$82.3M$82.3M$82.3M$82.3M$82.3M$82.3M$82.3M$82.3M
Intangible Assets0$133.0M$701.0M$710.5M$715.3M$724.8M$705.9M$379.5M$118.8M$388.8M
Total Assets$269.3M$391.7M$1.12B$1.62B$2.21B$1.94B$1.71B$1.90B$1.71B$2.90B
Accounts Payable$6.3M$15.3M$6.0M$10.3M$18.7M$23.0M$27.3M$6.0M$17.3M$45.5M
Short-term Debt00$11.7M$20.0M0$208.8M$72.1M$194.3M$257.8M$569.6M
Total Current Liabilities$49.6M$82.0M$166.8M$235.9M$277.3M$509.3M$406.2M$603.1M$581.0M$968.4M
Long-term Debt$98.2M$145.0M$141.3M$293.9M$309.1M$956.6M$1.26B$1.90B$2.11B$2.03B
Total Liabilities$149.8M$235.2M$768.5M$1.03B$1.73B$1.94B$2.05B$2.71B$2.80B$3.10B
Retained Earnings-$735.1M-$814.1M-$938.9M-$1.19B-$1.63B-$2.10B-$2.66B-$3.28B-$3.65B-$2.96B
Total Equity$119.6M$156.4M$350.7M$594.3M$482.0M$1.4M-$347.1M-$818.6M-$1.10B-$205.3M
Total Debt$98.2M$145.0M$153.0M$328.0M$420.4M$1.27B$1.46B$2.23B$2.47B$2.71B
Net Debt-$133.4M-$46.3M-$74.6M-$358.5M-$683.2M$496.0M$1.05B$1.35B$1.33B$761.7M
Working Capital$211.7M$167.0M$154.1M$543.4M$954.4M$445.0M$287.5M$615.5M$784.5M$1.31B

Balance Sheet (Quarterly)

Year2025-Q32025-Q42026-Q12026-Q2
Cash & Equivalents$672.6M$984.6M$834.0M$1.05B
Total Assets$2.64B$2.90B$2.87B$3.25B
Total Liabilities$2.80B$3.10B$3.05B$3.42B
Total Equity-$155.8M-$205.3M-$180.5M-$165.4M
Total Debt$410.1M$2.71B$395.1M$696.5M

Cash Flow (10y)

Year2016201720182019202020212022202320242025
Net Income-$142.1M-$79.0M-$128.1M-$251.6M-$438.2M-$523.9M-$559.0M-$626.6M-$363.3M$682.6M
Depreciation & Amortization$3.3M$17.7M$26.1M$32.2M$84.9M$64.1M$128.8M$236.6M$75.7M$38.8M
Stock-based Compensation$35.0M$30.6M$33.3M$42.1M$70.3M$103.5M$110.3M$131.2M$74.6M$74.5M
Change in Working Capital-$9.0M$13.2M$14.2M$20.4M$36.9M-$23.8M-$85.3M-$4.0M$102.5M-$47.9M
Operating Cash Flow-$103.6M-$10.1M-$27.6M-$98.6M-$194.1M-$251.3M-$356.7M-$158.4M-$107.7M$711.2M
Capital Expenditure-$1.8M-$3.1M-$15.5M-$45.4M-$56.0M-$85.3M-$152.5M-$120.6M-$74.2M-$300.0M
Acquisitions0-$77.2M-$48.9M-$4.0M$38.1M$57.1M$128.4M000
Stock Repurchased0000000000
Dividends Paid0000000000
Free Cash Flow-$105.3M-$13.2M-$43.2M-$144.1M-$250.0M-$336.7M-$509.1M-$279.0M-$181.9M$411.2M

Cash Flow (Quarterly)

Year2025-Q32025-Q42026-Q12026-Q2
Operating Cash Flow-$66.3M-$34.3M-$59.0M$129.1M
Capital Expenditure-$256.3M-$37.3M-$1.4M-$7.1M
Free Cash Flow-$322.6M-$71.6M-$60.4M$122.0M
Dividends Paid0000
Stock-based Compensation$19.4M$18.5M$23.4M$23.3M

Growth & Margins (10y)

Year2016201720182019202020212022202320242025
Revenue Growth (YoY)+135.0%+36.2%+16.0%+24.0%+41.4%+29.7%+34.2%-14.0%+114.5%
Net Income Growth (YoY)+44.4%-62.1%-96.4%-74.2%-19.6%-6.7%-12.1%+42.0%+287.9%
EPS Growth (YoY)+51.6%-36.1%-55.3%-55.5%-11.9%-4.8%-7.4%+43.5%+281.4%
Shares Change (YoY)+15.1%+18.9%+26.4%+12.2%+6.7%+1.8%+4.3%+2.7%+14.9%
FCF Growth (YoY)+87.5%-227.9%-233.7%-73.6%-34.6%-51.2%+45.2%+34.8%+326.0%
Gross Margin-42.2%97.6%95.2%96.0%95.0%94.0%93.6%93.0%92.9%95.9%
Operating Margin-159.7%-33.1%-43.7%-78.6%-113.4%-69.5%-64.0%-46.9%-37.5%49.5%
EBITDA Margin-155.7%-24.0%-33.8%-63.6%-79.6%-68.4%-52.6%-35.2%-14.9%51.3%
Net Margin-171.8%-40.6%-48.4%-82.0%-115.1%-97.3%-80.0%-66.8%-45.0%39.4%
FCF Margin-127.4%-6.8%-16.3%-46.9%-65.7%-62.5%-72.9%-29.8%-22.6%23.8%
Effective Tax Rate-0.4%-1.7%0.0%-4.9%-8.7%-1.1%4.8%10.0%-0.0%2.0%

Per-Share Data (10y)

Year2016201720182019202020212022202320242025
FCF Per Share$-3.09$-0.34$-0.93$-2.45$-3.79$-4.78$-7.10$-3.73$-2.37$4.66
Dividends Per Share$0.00$0.00$0.00$0.00$0.00$0.00$0.00$0.00$0.00$0.00
Shares Outstanding (Basic)$34.0M$39.1M$46.6M$58.9M$66.0M$70.5M$71.7M$74.8M$76.8M$79.5M

What to look at in Biotech

Most small biotechs lose money. Analysing them with P/E makes no sense — look at cash and pipeline.

Profitability

Return on Equity21.72%
Return on Invested Capital2.61%
Return on Assets-1.18%
Gross Margin82.14%
Operating Margin11.52%
Net Margin-3.80%

Financial Health

Debt / Equity-4.21
Current Ratio3.39

Key Ratios (10y)

Year2016201720182019202020212022202320242025
P/E-2.62-8.26-12.48-11.25-9.19-5.36-4.90-3.29-9.548.85
P/B3.114.174.564.768.361951.79-7.89-2.52-3.16-29.43
P/S4.493.366.049.2110.585.213.922.204.303.49
Gross Margin-42.2%97.6%95.2%96.0%95.0%94.0%93.6%93.0%92.9%95.9%
Operating Margin-159.7%-33.1%-43.7%-78.6%-113.4%-69.5%-64.0%-46.9%-37.5%49.5%
Net Margin-171.8%-40.6%-48.4%-82.0%-115.1%-97.3%-80.0%-66.8%-45.0%39.4%

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